AddFabry Disease Treatment Divided based on the kind of treatment into substrate reduction therapy (SRT), chaperone treatment, enzyme replacement therapy (ERT), and others. Enzyme replacement therapy is the norm for illness management. Even though both ERTs, Fabrazyme by Sanofi and Replagal by Shire, are approved in Europe, only Fabrazyme is in the US.
The most prevalent lysosomal storage illness is Divided based on the kind of treatment into substrate reduction therapy (SRT), chaperone treatment, enzyme replacement therapy (ERT), and others. Enzyme replacement therapy is the norm for illness management. Even though both ERTs, Fabrazyme by Sanofi and Replagal by Shire, are approved in Europe, only Fabrazyme is in the US.
Fabry Disease Treatment Fabry-specific and non-Fabry-specific treatments are available as alternatives for treatment. Both migalastat hydrochloride, an oral pharmacological chaperone that corrects the folding of mutant alpha-Gal A in patients with Fabry disease and amenable alpha-Gal A mutations, and recombinant alpha-galactosidase A (alpha-Gal A), the enzyme that is deficient in patients with Fabry disease, are available as Fabry-specific treatments. It is unknown how these treatments will affect mortality. description for your Article from here.
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